Targeted replacement of full-length CFTR in human airway stem cells by CRISPR/CAS9 for pan-mutation correction in the endogenous locus
Referente attività: Fiorentina Ascenzioni
Area di intervento: Salute pubblica e benessere
Durata dell’iniziativa: 2022-01-01
articolo divulgativo per Orizzonti FC, Rubrica La capsula del tempo, raccontare al pubblico: "Targeted replacement of full-length CFTR in human airway stem cells by CRISPR/CAS9 for pan-mutation correction in the endogenous locus"